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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Dystrophie musculaire de Becker
DMD
Metabolism
Dystrophine
Cell Biology
Delivery
Muscle Biology
Antisense oligonucleotides
Calcium Channels
Génomique
LncARN
Humans
Dynamin 2
Liver
Diseases
Becker BMD muscular dystrophy
LncRNA
Mitochondrial fission
Dystrophie Musculaire de Duchenne DMD
Clinical trials
Duchenne DMD dystrophy
Muscles/physiopathology
Inbred C57BL
Dystrophin
Duchenne muscular dystrophy DMD
CaVβs
Cardiomyopathy
Multiresolution modeling
Drp1
Molecular Sequence Data
Centronuclear myopathy
Homeostasis
MES
Hepatocellular carcinoma
Gene modifiers
Muscle development
L-Type
BMD
Immunoglobulin Fc Fragments/pharmacology
Activin Receptors
Inhibitors
Animals
Knockout
Exon skipping
Cultured
LKB1
Inbred mdx
Myogenesis
Dystrophy
Autophagy
CaV subunits
Becker muscular dystrophy
Hear
Muscle Strength
Multi exon skipping
Genomic
Mdx mouse
Skeletal muscle
Cell Line
Morphogenesis
DMO
Epigenetics
Animal/physiopathology
DHPR α1S
Male
Dystrophin-EGFP
Energy Metabolism/drug effects
Cachexia
MiARN
Cardiomyopathie
Base Sequence
Cells
Multi resolution modeling
Cell homeostasis
CTNNB1
Allele‐specific silencing therapy
NAD+
CD38
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Invivo
Muscular dystrophy
Muscle
Muscular Dystrophy
Long QT
Becker muscular dystrophy BMD
NNOS
Dystrophin central domain
Dystrophie Musculaire de Becker BMD
Human Umbilical Vein Endothelial Cells
Muscular Atrophy
Myotendinous junction
Calcium
Gene expression
Duchenne muscular dystrophy
Modificateurs de gènes
Long noncoding RNA
Molecular docking
Gene Expression Regulation/drug effects
Mice
Ex-vivo